Blastic plasmacytoid dendritic cell neoplasm (BPDCN)

Active Ingredient: Tagraxofusp

Indication for Tagraxofusp

Population group: only adults (18 years old or older)
Therapeutic intent: Curative procedure

ELZONRIS is indicated as monotherapy for the first-line treatment of adult patients with blastic plasmacytoid dendritic cell neoplasm (BPDCN).

For this indication, competent medicine agencies globally authorize below treatments:

12 ug/kg once daily on days 1-5 of a 21-day cycle

For:

Dosage regimens

Intravenous, 12 micrograms tagraxofusp per kilogram of body weight, once daily, 5 doses in total, over the duration of 21 days.

Detailed description

The recommended dose is 12 mcg/kg tagraxofusp administered as an intravenous infusion over 15 minutes, once daily, on days 1-5 of a 21-day cycle. The dosing period may be extended for dose delays up to day 10 of the cycle. Treatment should be continued until disease progression or unacceptable toxicity.

First treatment cycle

The first cycle of tagraxofusp should be administered in the in-patient setting. Patients should be monitored for signs and symptoms of hypersensitivity or capillary leak syndrome until at least 24 hours after the last infusion.

Subsequent treatment cycles

Tagraxofusp can be administered in the in-patient setting or in a suitable out-patient ambulatory care setting that is equipped for intensive monitoring of patients with haematopoietic malignancies undergoing treatment.

Pre-medication

Patients should be pre-medicated with a H1-histamine antagonist (e.g. diphenhydramine hydrochloride), a H2-histamine antagonist, a corticosteroid (e.g. 50 mg intravenous methylprednisolone or equivalent) and paracetamol approximately 60 minutes prior to the start of infusion.

Dose adjustments

Vital signs should be monitored and albumin, transaminases, and creatinine checked prior to preparing each dose of tagraxofusp. See Table 1 for recommended dose modifications and Table 2 for capillary leak syndrome (CLS) management guidelines.

Vital signs should be monitored frequently during dosing.

Table 1. Recommended tagraxofusp dosing regimen modifications:

ParameterSeverity criteriaDose modification
Serum albuminSerum albumin < 3.5 g/dL or reduced
≥ 0.5 g/dL from value measured prior to
initiation of the current cycle
See CLS Management Guidelines (Table 2)
Body weightBody weight increase ≥ 1.5 kg over pre-
treatment weight on prior treatment day
See CLS Management Guidelines (Table 2)
Aspartate
aminotransferase
(AST) or alanine
aminotransferase
(ALT)
ALT or AST increase > 5 times the
upper limit of normal
Withhold treatment until transaminase
elevations are ≤ 2.5 times the upper limit of
normal.
Serum creatinineSerum creatinine > 1.8 mg/dL
(159 micromol/L) or creatinine
clearance < 60 mL/minute
Withhold treatment until serum creatinine
resolves to ≤ 1.8 mg/dL (159 micromol/L) or
creatinine clearance ≥ 60 mL/minute.
Systolic blood
pressure
Systolic blood pressure ≥ 160 mmHg or
≤ 80 mmHg
Withhold treatment until systolic blood
pressure is < 160 mmHg or > 80 mmHg.
Heart rateHeart rate ≥ 130 bpm or ≤ 40 bpmWithhold treatment until heart rate is
< 130 bpm or > 40 bpm.
Body temperatureBody temperature ≥ 38°CWithhold treatment until body temperature is
< 38°C.
Hypersensitivity
reactions
Mild or moderateWithhold treatment until resolution of any
mild or moderate hypersensitivity reaction.
Resume tagraxofusp at the same infusion
rate.

Table 2. CLS management guidelines:

Time of
Presentation
CLS
Sign/Symptom
Recommended
Action
Tagraxofusp
Dosing
Management
Prior to first dose of
tagraxofusp
in cycle 1
Serum albumin < 3.2 g/dLAdminister tagraxofusp when serum albumin ≥ 3.2 g/dL
During tagraxofusp
dosing
Serum albumin < 3.5 g/dLAdminister 25 g intravenous albumin
every 12 hours (or more frequently as
practical) until serum albumin is
≥ 3.5 g/dL AND not reduced by
≥ 0.5 g/dL from the value measured
prior to dosing initiation of the current
cycle
Hold dosing
until the
relevant CLS
sign/symptom
has resolved1
Serum albumin reduced by
≥ 0.5 g/dL from the
albumin value measured
prior to tagraxofusp dosing
initiation of the current
cycle
A pre-dose body weight
that is increased by ≥ 1.5 kg
over the previous day's
pre-dose weight
Administer 25 g intravenous albumin
(every 12 hours or more frequently as
practical), and manage fluid status as
indicated clinically (e.g., generally
with intravenous fluids and
vasopressors if hypotensive and with
diuretics if normotensive or
hypertensive), until body weight
increase has resolved (i.e. the increase
is no longer ≥ 1.5 kg greater than the
previous day's pre-dose weight).
Oedema, fluid overload
and/or hypotension
Administer 25 g intravenous albumin
(every 12 hours, or more frequently as
practical) until serum albumin is
≥ 3.5 g/dL.

Administer 1 mg/kg of
methylprednisolone (or an equivalent)
per day, until resolution of CLS
sign/symptom or as indicated
clinically.

Aggressive management of fluid status
and hypotension if present, which
could include intravenous fluids and/or
diuretics or other blood pressure
management, until resolution of CLS
sign/symptom or as clinically
indicated.

1 If tagraxofusp dose is held:
* Tagraxofusp administration may resume in the same cycle if all CLS signs/symptoms have resolved and the patient did not require measures to treat haemodynamic instability.
* Administration should be held for the remainder of the cycle if CLS signs/symptoms have not resolved or the patient required measures to treat haemodynamic instability (e.g., required administration of intravenous fluids and/or vasopressors to treat hypotension) (even if resolved).
* Administration may only resume in the next cycle if all CLS signs/symptoms have resolved, and the patient is haemodynamically stable.

Dosage considerations

Tagraxofusp is for intravenous use.

The prepared dose of diluted tagraxofusp should be administered via an infusion syringe pump over 15 minutes. The total infusion time should be controlled using an infusion syringe pump to deliver the entire dose and the sodium chloride 9 mg/mL (0.9%) solution for injection within 15 minutes.

Tagraxofusp must not be administered as an intravenous push or bolus. It should be administered through a dedicated intravenous line and it must not be mixed with other medicinal products.

Prior to infusion, venous access should be established and maintained with sodium chloride 9 mg/mL (0.9%) solution for injection.

Active ingredient

Tagraxofusp

Tagraxofusp is a CD123-directed cytotoxin composed of recombinant human interleukin-3 (IL-3) and truncated diphtheria toxin (DT) fusion protein that targets CD123-expressing cells. Tagraxofusp irreversibly inhibits protein synthesis of target cells by inactivating elongation factor 2 (EF2), resulting in apoptosis (cell death).

Read more about Tagraxofusp

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