Miglustat is indicated for the oral treatment of adult patients with mild to moderate type 1 Gaucher disease. Miglustat may be used only in the treatment of patients for whom enzyme replacement therapy is unsuitable.
For this indication, competent medicine agencies globally authorize below treatments:
Oral
100 - 300 mg
From 33.333 To 100 mg 3 time(s) per day every day
300 mg
The recommended starting dose for the treatment of adult patients with type 1 Gaucher disease is 100 mg three times a day.
Temporary dose reduction to 100 mg once or twice a day may be necessary in some patients because of diarrhoea.
Miglustat can be taken with or without food.