The World Health Organization's ATC classification organizes medical drugs based on therapeutic properties, chemical composition, and anatomy. It helps make essential medicines readily available globally and is widely used in the pharmaceutical industry.
| Level | Code | Title | |
|---|---|---|---|
1
|
M | Musculo-skeletal system | |
2
|
M09 | Other drugs for disorders of the musculo-skeletal system | |
3
|
M09A | Other drugs for disorders of the musculo-skeletal system | |
4
|
M09AX | Other drugs for disorders of the musculo-skeletal system | |
5
|
M09AX13 |
| Active Ingredient |
|---|
|
Casimersen is designed to bind to exon 45 of dystrophin pre-mRNA resulting in exclusion of this exon during mRNA processing in patients with genetic mutations that are amenable to exon 45 skipping. Exon 45 skipping is intended to allow for production of an internally truncated dystrophin protein in patients with genetic mutations that are amenable to exon 45 skipping. |
| Document | Type | Information Source | |
|---|---|---|---|
| AMONDYS 45 Solution for injection | MPI, US: SPL/PLR | FDA, National Drug Code (US) |