Advanced RET fusion-positive solid tumours

Active Ingredient: Selpercatinib

Indication for Selpercatinib

Population group: only children (1 year - 12 years old) , adolescents (12 years - 18 years old) , adults (18 years old or older)
Therapeutic intent: Curative procedure

Selpercatinib as monotherapy is indicated for the treatment of adults and paediatric patients 2 years of age and older with advanced RET fusion-positive solid tumours, when treatment options not targeting RET provide limited clinical benefit, or have been exhausted.

For this indication, competent medicine agencies globally authorize below treatments:

For patients weighting <50 kg 120 mg twice daily and for patients weighting ≥50 kg 160 mg twice daily

For:

Dosage regimens

Regimen A, in the case that patient weight is < 50 kg :

Oral, 120 milligrams selpercatinib, 2 times daily.

Regimen B, in the case that patient weight is ≥ 50 kg :

Oral, 160 milligrams selpercatinib, 2 times daily.

Detailed description

The recommended dose of selpercatinib for patients 12 years of age and older based on body weight is:

  • Less than 50 kg: 120 mg twice daily.
  • 50 kg or greater: 160 mg twice daily.

If a patient vomits or misses a dose, the patient should be instructed to take the next dose at its scheduled time; an additional dose should not be taken.

Treatment should be continued until disease progression or unacceptable toxicity.

The current selpercatinib dose should be reduced by 50% if co-administering with a strong CYP3A inhibitor. If the CYP3A inhibitor is discontinued, the selpercatinib dose should be increased (after 3-5 half-lives of the inhibitor) to the dose that was used before starting the inhibitor.

Dose adjustments

Management of some adverse reactions may require dose interruption and/or dose reduction. Selpercatinib dose modifications are summarised in Table 1 and Table 2.

Table 1. Recommended dose modifications for selpercatinib for adverse reactions based on body weight:

Dose
modification
Adults and
adolescents
≥50 Kg
Adults and
adolescents
<50 Kg
Starting
dose
160 mg orally
twice daily
120 mg orally
twice daily
First dose
reduction
120 mg orally
twice daily
80 mg orally
twice daily
Second dose
reduction
80 mg orally
twice daily
40 mg orally
twice daily
Third dose
reduction*
40 mg orally
twice daily
Not applicable

* Permanently discontinue selpercatinib in patients unable to tolerate three dose reductions

Dose modifications in paediatric patients for adverse reactions should be determined based on the current dose and step wise dose-level modification approach as that described for adults in the adverse reactions discussed below (Table 2) except where stated otherwise.

Table 2. Recommended dose modifications for adverse reactions:

Adverse drug
reaction (ADR)
 Dose modification
Increased alanine
aminotransferase
(ALT) or aspartate
aminotransferase
(AST)
Grade 3 or Grade 4• Suspend dose until toxicity resolves
to baseline.
Resume at a dose reduced by
2 levels.
• If after at least 2 weeks selpercatinib
is tolerated without recurrent
increased ALT or AST, increase
dosing by 1 dose level.
• If selpercatinib is tolerated without
recurrence for at least 4 weeks,
increase to dose taken prior to the
onset of Grade 3 or 4 increased AST
or ALT.
• Permanently discontinue
selpercatinib if Grade 3 or 4 ALT or
AST increases recur despite dose
modifications.
HypersensitivityAll Grades• Suspend dose until toxicity resolves
and begin corticosteroids at a dose of
1 mg/kg.
Resume selpercatinib at 40 mg twice
daily while continuing steroid
treatment. Discontinue selpercatinib
for recurrent hypersensitivity.
• If after at least 7 days, selpercatinib
is tolerated without recurrent
hypersensitivity, incrementally
increase the selpercatinib dose by
1 dose level each week, until the
dose taken prior to the onset of
hypersensitivity is reached. Taper
steroid dose after selpercatinib has
been tolerated for at least 7 days at
the final dose.
QT interval
prolongation
Grade 3• Suspend dose for QTcF intervals
>500 ms until the QTcF returns to
<470 ms (or ≤440 ms for patients
under 12 years of age) or baseline.
• Resume selpercatinib treatment at
the next lower dose level.
Grade 4• Permanently discontinue
selpercatinib if QT prolongation
remains uncontrolled after two dose
reductions or if the patient has signs
or symptoms of serious arrhythmia.
HypertensionGrade 3• Patient blood pressure should be
controlled before starting treatment.
• Selpercatinib should be suspended
temporarily for medically significant
hypertension until controlled with
antihypertensive therapy. Dosing
should be resumed at the next lower
dose if clinically indicated.
Grade 4• Selpercatinib should be discontinued
permanently if medically significant
hypertension cannot be controlled.
Haemorrhagic
events
Grade 3• Selpercatinib should be suspended
until recovery to baseline. Resume at
a reduced dose.
If Grade 3 events reoccur following
dose modification, permanently
discontinue selpercatinib.
Grade 4• Permanently discontinue
selpercatinib.
Interstitial lung
disease
(ILD)/Pneumonitis
Grade 2• Withhold selpercatinib until
resolution.
• Resume at a reduced dose.
• Discontinue selpercatinib for
recurrent ILD/pneumonitis
Grade 3 or Grade 4• Discontinue selpercatinib.
Other adverse
reactions
Grade 3 or Grade 4• Selpercatinib should be suspended
until recovery to baseline. Resume at
a reduced dose.
• If Grade 4 events reoccur following
dose modification, permanently
discontinue selpercatinib.

Elderly

No dose adjustment is required based on age.

No overall differences were observed in the treatment emergent adverse events or effectiveness of selpercatinib between patients who were ≥65 years of age and younger patients. Limited data are available in patients ≥75 years.

Dosage considerations

Patients should take the doses at approximately the same time every day.

Selpercatinib must be accompanied by a meal if used concomitantly with a proton pump inhibitor.

Selpercatinib should be administered 2 hours before or 10 hours after H2 receptor antagonists.

40 mg 3 times daily or 80-160 mg twice daily based on body surface area (BSA)

For:

Dosage regimens

Regimen A, in the case that patient age in years is ≥ 2 and patient body surface area is ≥ 0.45 m² and patient body surface area is ≤ 0.65 m² :

Oral, 40 milligrams selpercatinib, 3 times daily.

Regimen B, in the case that patient age in years is ≥ 2 and patient body surface area is ≥ 0.66 m² and patient body surface area is ≤ 1.08 m² :

Oral, 80 milligrams selpercatinib, 2 times daily.

Regimen C, in the case that patient age in years is ≥ 2 and patient body surface area is ≥ 1.09 m² and patient body surface area is ≤ 1.52 m² :

Oral, 120 milligrams selpercatinib, 2 times daily.

Regimen D, in the case that patient age in years is ≥ 2 and patient body surface area is ≥ 1.53 m² :

Oral, 160 milligrams selpercatinib, 2 times daily.

Detailed description

The recommended dose of selpercatinib for paediatric patients 2 to less than 12 years of age is based on the following body surface area (BSA) categories:

Table 1. Recommended dose for paediatric patients 2 to less than 12 years of age:

Body surface area (BSA)Recommended dose
0.45 to 0.65 m²40 mg three times daily
0.66 to 1.08 m²80 mg twice daily
1.09 to 1.52 m²120 mg twice daily
≥1.53 m²160 mg twice daily

If a patient vomits or misses a dose, the patient should be instructed to take the next dose at its scheduled time; an additional dose should not be taken.

Treatment should be continued until disease progression or unacceptable toxicity.

The current selpercatinib dose should be reduced by 50% if co-administering with a strong CYP3A inhibitor. If the CYP3A inhibitor is discontinued, the selpercatinib dose should be increased (after 3-5 half-lives of the inhibitor) to the dose that was used before starting the inhibitor.

Dose adjustments

Management of some adverse reactions may require dose interruption and/or dose reduction. Selpercatinib dose modifications are summarised in Table 2 and Table 3.

Table 2. Recommended dose modifications for selpercatinib for adverse reactions based on body weight:

Dose
modification
Adults and
adolescents
≥50 Kg
Adults and
adolescents
<50 Kg
Starting
dose
160 mg orally
twice daily
120 mg orally
twice daily
First dose
reduction
120 mg orally
twice daily
80 mg orally
twice daily
Second dose
reduction
80 mg orally
twice daily
40 mg orally
twice daily
Third dose
reduction*
40 mg orally
twice daily
Not applicable

* Permanently discontinue selpercatinib in patients unable to tolerate three dose reductions

Dose modifications in paediatric patients for adverse reactions should be determined based on the current dose and step wise dose-level modification approach as that described for adults in the adverse reactions discussed below (Table 3) except where stated otherwise.

Table 3. Recommended dose modifications for adverse reactions:

Adverse drug
reaction (ADR)
 Dose modification
Increased alanine
aminotransferase
(ALT) or aspartate
aminotransferase
(AST)
Grade 3 or Grade 4• Suspend dose until toxicity resolves
to baseline.
Resume at a dose reduced by
2 levels.
• If after at least 2 weeks selpercatinib
is tolerated without recurrent
increased ALT or AST, increase
dosing by 1 dose level.
• If selpercatinib is tolerated without
recurrence for at least 4 weeks,
increase to dose taken prior to the
onset of Grade 3 or 4 increased AST
or ALT.
• Permanently discontinue
selpercatinib if Grade 3 or 4 ALT or
AST increases recur despite dose
modifications.
HypersensitivityAll Grades• Suspend dose until toxicity resolves
and begin corticosteroids at a dose of
1 mg/kg.
Resume selpercatinib at 40 mg twice
daily while continuing steroid
treatment. Discontinue selpercatinib
for recurrent hypersensitivity.
• If after at least 7 days, selpercatinib
is tolerated without recurrent
hypersensitivity, incrementally
increase the selpercatinib dose by
1 dose level each week, until the
dose taken prior to the onset of
hypersensitivity is reached. Taper
steroid dose after selpercatinib has
been tolerated for at least 7 days at
the final dose.
QT interval
prolongation
Grade 3• Suspend dose for QTcF intervals
>500 ms until the QTcF returns to
<470 ms (or ≤440 ms for patients
under 12 years of age) or baseline.
• Resume selpercatinib treatment at
the next lower dose level.
Grade 4• Permanently discontinue
selpercatinib if QT prolongation
remains uncontrolled after two dose
reductions or if the patient has signs
or symptoms of serious arrhythmia.
HypertensionGrade 3• Patient blood pressure should be
controlled before starting treatment.
• Selpercatinib should be suspended
temporarily for medically significant
hypertension until controlled with
antihypertensive therapy. Dosing
should be resumed at the next lower
dose if clinically indicated.
Grade 4• Selpercatinib should be discontinued
permanently if medically significant
hypertension cannot be controlled.
Haemorrhagic
events
Grade 3• Selpercatinib should be suspended
until recovery to baseline. Resume at
a reduced dose.
If Grade 3 events reoccur following
dose modification, permanently
discontinue selpercatinib.
Grade 4• Permanently discontinue
selpercatinib.
Interstitial lung
disease
(ILD)/Pneumonitis
Grade 2• Withhold selpercatinib until
resolution.
• Resume at a reduced dose.
• Discontinue selpercatinib for
recurrent ILD/pneumonitis
Grade 3 or Grade 4• Discontinue selpercatinib.
Other adverse
reactions
Grade 3 or Grade 4• Selpercatinib should be suspended
until recovery to baseline. Resume at
a reduced dose.
• If Grade 4 events reoccur following
dose modification, permanently
discontinue selpercatinib.

Dosage considerations

Patients should take the doses at approximately the same time every day.

Selpercatinib must be accompanied by a meal if used concomitantly with a proton pump inhibitor.

Selpercatinib should be administered 2 hours before or 10 hours after H2 receptor antagonists.

Active ingredient

Selpercatinib

Selpercatinib is an inhibitor of the rearranged during transfection (RET) receptor tyrosine kinase. Selpercatinib inhibited wild-type RET and multiple mutated RET isoforms as well as VEGFR1 and VEGFR3 with IC50 values ranging from 0.92 nM to 67.8 nM. In in vitro and in vivo tumor models, selpercatinib demonstrated anti-tumor activity in cells harboring constitutive activation of RET protein resulting from gene fusions and mutations, including CCDC6-RET, KIF5B-RET, RET V804M, and RET M918T.

Read more about Selpercatinib

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