Severe hepatic veno-occlusive disease (VOD) in haematopoietic stem-cell transplantation (HSCT)

Active Ingredient: Defibrotide

Indication for Defibrotide

Population group: only minors (0 - 18 years old) , adults (18 years old or older)
Therapeutic intent: Curative procedure

Defibrotide is indicated for the treatment of severe hepatic veno-occlusive disease (VOD) also known as sinusoidal obstruction syndrome (SOS) in haematopoietic stem-cell transplantation (HSCT) therapy.

It is indicated in adults and in adolescents, children and infants over 1 month of age.

For this indication, competent medicine agencies globally authorize below treatments:

6.25 mg/kg body weight every 6 hours for a minimum of 21 days

For:

Dosage regimens

Intravenous, 6.25 milligrams defibrotide per kilogram of body weight, once every 6 hours, over the duration of 21 days.

Detailed description

The recommended dose is 6.25 mg/kg body weight every 6 hours (25 mg/kg/day).

There is limited efficacy and safety data on doses above this level and consequently it is not recommended to increase the dose above 25 mg/kg/day.

The treatment should be administered for a minimum of 21 days and continued until the symptoms and signs of severe VOD resolve.

Active ingredient

Defibrotide

Defibrotide is an oligonucleotide mixture with demonstrated antithrombotic, fibrinolytic, anti-adhesive and anti-inflammatory actions. The mechanism of action is multifactorial. It primarily acts through reducing excessive endothelial cell (EC) activation (endothelial dysfunction), modulating endothelial homeostasis as well as restoring thrombo-fibrinolytic balance. However, the exact mechanism of action of defibrotide is not fully elucidated.

Read more about Defibrotide

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