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Ataluren

Description

A nonsense mutation in DNA results in a premature stop codon within an mRNA. This premature stop codon in the mRNA causes disease by terminating translation before a full-length protein is generated. Ataluren enables ribosomal readthrough of mRNA containing such a premature stop codon, resulting in production of a full-length protein.

ATC Classification

Code
Title
Category
M09AX03
Ataluren
M Musculo-skeletal system → M09 Other drugs for disorders of the musculo-skeletal system → M09A Other drugs for disorders of the musculo-skeletal system → M09AX Other drugs for disorders of the musculo-skeletal system

Trade names

Trade name
Countries

Austria Netherlands

Product Monographs

Monograph
Type
Country
TRANSLARNA Granules for oral suspension
MPI, EU: SmPC