BYSANTI Tablet Ref.[116258] Active ingredients: Milsaperidone

Source: FDA, National Drug Code (US)  Revision Year: 2026 

4. Contraindications

BYSANTI is contraindicated in individuals with a known hypersensitivity reaction to milsaperidone or the inactive ingredients in BYSANTI. Anaphylaxis, angioedema, and other hypersensitivity reactions have been reported [see Adverse Reactions (6.2)].

5. Warnings and Precautions

5.1 Increased Mortality in Elderly Patients with Dementia-Related Psychosis

Elderly patients with dementia-related psychosis treated with antipsychotic drugs are at an increased risk of death. Analyses of 17 placebo-controlled trials (modal duration of 10 weeks) largely in patients taking atypical antipsychotic drugs for dementia-related psychosis, revealed a risk of death in antipsychotic drug-treated patients was 1.6 to 1.7 times the risk of death in placebo-treated patients. Over the course of a typical 10-week controlled trial, the incidence of death in antipsychotic drug-treated patients was about 4.5%, compared to an incidence of about 2.6% in placebo-treated patients. Although the causes of death were varied, most of the deaths appeared to be either cardiovascular (e.g., heart failure, sudden death) or infectious (e.g., pneumonia) in nature.

BYSANTI is not approved for the treatment of patients with dementia-related psychosis [see Indications and Usage (1)].

5.2 Cerebrovascular Adverse Reactions, Including Stroke, in Elderly Patients with Dementia-Related Psychosis

In placebo-controlled trials in elderly patients with dementia-related psychosis treated with risperidone, aripiprazole, or olanzapine had a higher incidence of stroke and transient ischemic attack, including fatal stroke compared to those treated with placebo.

BYSANTI is not approved for the treatment of patients with dementia-related psychosis [see Indications and Usage (1)].

5.3 QTc Interval Prolongation

In a QTc study, the use of iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) was associated with QTc interval prolongation, especially with concomitant use of a CYP2D6 inhibitor or a CYP3A4 inhibitor. No cases of torsade de pointes or other severe cardiac arrhythmias were observed in the iloperidone studies.

Risk Factors for Clinically Significant Risks of QTc Interval Prolongation

Certain circumstances may increase the risk of torsade de pointes and/or sudden death in association with the use of drugs that prolong the QTc interval, including ischemic cardiomyopathy; hypokalemia; genetic predisposition, concomitant use of other drugs that prolong the QTc interval or increases the exposure of the drug; and elevated baseline QTc interval.

Steps to Prevent or Mitigate Clinically Significant Adverse Reactions or Risks Associated with QTc Interval Prolongation

The concomitant use of BYSANTI should be avoided with other drugs that prolong the QTc interval including Class 1A antiarrhythmics (e.g., quinidine, procainamide) or Class III antiarrhythmics (e.g., amiodarone, sotalol), antipsychotic drugs that prolong the QTc interval (e.g., chlorpromazine, thioridazine), antibiotics that prolong the QTc interval (e.g., gatifloxacin, moxifloxacin), or any other class of drugs known to prolong the QTc interval (e.g., pentamidine, levomethadyl acetate, methadone). BYSANTI should also be avoided in other patients with significant risk of developing torsades de pointes including those with congenital long QT syndrome, recent myocardial infarction, ischemic cardiomyopathy, unstable angina, bradyarrhythmias, uncontrolled hypertension, high degree atrioventricular block, severe aortic stenosis, or uncontrolled hypothyroidism.

When BYSANTI is used concomitantly with other drugs (e.g., strong CYP2D6 inhibitors, strong CYP3A4 inhibitors, and taking both a CYP2D6 inhibitor and a CYP3A4 inhibitor) [see Drug Interactions (7.1)] or in patients with decreased activity of CYP2D6 [see Clinical Pharmacology (12.5)] decrease the BYSANTI dosage [see Dosage and Administration (2.x)].

Patients being considered for BYSANTI treatment who are at risk for significant electrolyte disturbances should have baseline serum potassium and magnesium measurements with periodic monitoring because hypokalemia (and/or hypomagnesemia) may increase the risk of QTc interval prolongation and arrhythmia.

BYSANTI should be discontinued in patients who are found to have persistent QTc measurements >500 msec. If patients taking BYSANTI experience symptoms that could indicate the occurrence of arrhythmias, e.g., dizziness, palpitations, or syncope, the health care provider should initiate further evaluation, including cardiac monitoring.

5.4 Neuroleptic Malignant Syndrome

Neuroleptic Malignant Syndrome (NMS), a potentially fatal symptom complex, has been reported in association with administration of antipsychotic drugs, including iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo). Clinical manifestations of NMS include hyperpyrexia, muscle rigidity, altered mental status (including catatonic signs), and evidence of autonomic instability (irregular pulse or blood pressure, tachycardia, diaphoresis, and cardiac dysrhythmia). Additional signs may include elevated creatine phosphokinase, myoglobinuria (rhabdomyolysis), and acute renal failure.

If NMS is suspected, immediately discontinue BYSANTI and provide intensive symptomatic treatment and monitoring.

5.5 Tardive Dyskinesia

Tardive dyskinesia (TD), may develop in patients treated with antipsychotic drugs, including BYSANTI. TD can develop after relatively brief treatment period at low dosages and may also occur after discontinuation of treatment. If antipsychotic drug treatment is discontinued, TD may partially or completely remission. Antipsychotic treatment, however, may suppress or partially suppress the signs and symptoms of TD, possibly masking the underlying process. The effect that symptomatic suppression has upon the long-term course of TD is unknown.

The TD risk in patients treated with antipsychotic drugs appears to be highest among the elderly, especially elderly women, but it is impossible to predict, which patients will develop TD. The risk of developing TD and the likelihood that TD will become irreversible increase with the duration of antipsychotic drug treatment and the cumulative dosage.

In patients who require chronic antipsychotic drug treatment, use the lowest dosage and the shortest duration of treatment producing a satisfactory clinical response. Periodically reassess the need for continued treatment. If signs and symptoms of TD appear in a BYSANTI-treated patient, consider drug discontinuation. However, some patients may require BYSANTI treatment despite the presence of TD.

5.6 Metabolic Changes

Atypical antipsychotic drugs have caused metabolic changes (e.g., hyperglycemia, dyslipidemia, and body weight gain) that may increase cardiovascular/cerebrovascular risk.

Hyperglycemia and Diabetes Mellitus

Hyperglycemia, in some cases extreme and associated with ketoacidosis or hyperosmolar coma or death, has been reported in patients treated with atypical antipsychotics including iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo). Assess fasting plasma glucose before or soon after initiation BYSANTI and monitor periodically during long-term treatment.

Schizophrenia: In a 4-week fixed-dose placebo-controlled study of adults with schizophrenia (Study 2) [see Clinical Studies (14.1)], the mean change from baseline in serum glucose was 6.6 mg/dL and 0.5 mg/dL for iloperidone and placebo-treated patients, respectively. The proportion of patients with shifts in fasting glucose from normal (<100 mg/dL) to high (≥126 mg/dL) were 10.7% and 2.5% for the iloperidone- and placebo-treated patients, respectively.

In pooled analyses from clinical studies, for adults with schizophrenia who remained on treatment with iloperidone 10- 16 mg/day glucose increased, on average, from baseline by 1.8 mg/dL at 3-6 months (N=773), by 5.4 mg/dL at 6-12 months (N=723), and by 5.4 mg/dL at >12 months (N=425) of treatment. In a smaller subpopulation of patients who remained on treatment with iloperidone 20-24 mg/day, glucose decreased by 3.6 mg/dL at 3-6 months (N=34); by 9 mg/dL at 6-12 months (N=31), and by 18 mg/dL at > 12 months (N=20) of treatment.

Bipolar Mania: In a 4-week fixed dose study of adults with bipolar mania (Study 4) [see Clinical Studies (14.2)], mean changes from baseline in serum glucose and the proportion of patients with shifts in fasting glucose from Normal (<100 mg/dL) to High (≥126 mg/dL) for iloperidone-treated patients placebo-treated patients were similar.

Dyslipidemia

Undesirable alterations in lipids have been observed in patients treated with atypical antipsychotics. Before or soon after initiation of antipsychotic drugs, obtain a fasting lipid profile at baseline and monitor periodically during treatment.

Schizophrenia: In a 4-week fixed dose study of adults with schizophrenia (Study 2), the mean change from baseline in fasted total cholesterol was 8.2 mg/dL and 2.2 mg/dL for iloperidone and placebo-treated patients, respectively. The effects on LDL were similar to those on total cholesterol (changes of 9 mg/dL and 1.4 mg/dL for iloperidone and placebo-treated patients, respectively). Mean changes from baseline in fasted triglycerides were 0.8 mg/dL and 16.5 mg/dL for iloperidone and placebo-treated patients, respectively.

The proportion of patients with shifts from normal to high fasted total cholesterol, LDL, and triglycerides were similar for iloperidone- and placebo-treated patients. The proportion of patients with shifts in fasted HDL from normal (≥40 mg/dL) to low (<40 mg/dL) was greater for placebo-treated patients (23.8%) compared to iloperidone-treated (12.1%).

In pooled analysis from clinical studies, for adults with schizophrenia who remained on treatment with iloperidone, on average, both cholesterol and triglycerides decreased from baseline for those who remained on treatment at 3-6 months, 6-12 months, and >12-month time points in both 10-16 mg/day and 20-24 mg/day dosing groups.

Bipolar Mania: In a 4-week fixed dose study of adults with bipolar mania (Study 4), the mean changes from baseline for fasted total cholesterol, LDL, HDL, and triglycerides for iloperidone-treated patients were similar to those for placebo-treated patients. The proportion of patients with shifts in fasted total cholesterol from normal (<200 mg/dL) to high (≥240 mg/dL) was greater for iloperidone-treated patients (10.7%) than placebo-treated patients (7.2%). Shifts from normal to high LDL and triglycerides and from normal to low HDL occurred at rates for iloperidone-treated patients similar to those for placebo treated patients.

Weight Gain

Weight gain has been observed with atypical antipsychotic use. Monitor weight at baseline and frequently thereafter.

Schizophrenia: Across all short- and long-term studies of adults with schizophrenia, the overall mean increase in weight in iloperidone-treated patients from baseline at endpoint was 2.1 kg.

In 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies in adults with schizophrenia the mean change in weight was -0.1 kg, 2 kg, and 2.7 kg for the placebo, iloperidone 10-16 mg/day, and iloperidone 20-24 mg/day groups, respectively. The proportion of patients with >7% increase in weight from baseline was 4%, 12%, and 18% for placebo, iloperidone 10-16 mg/day, and iloperidone 20-24 mg/day groups, respectively.

Bipolar Mania: In a 4-week fixed dose study of adults with bipolar mania (Study 4), the mean increase in weight was 1.6 kg and 4.6 kg for the placebo and iloperidone 24 mg/day groups, respectively. The proportion of patients with ≥7% increase in weight from baseline was 14% and 35%, in the placebo and iloperidone 24 mg/day groups, respectively.

5.7 Orthostatic Hypotension and Syncope

BYSANTI can induce orthostatic hypotension associated with dizziness, tachycardia, and syncope. This reflects its alpha1-adrenergic antagonist properties.

  • In double-blind placebo-controlled short-term studies in patients with schizophrenia, where the dosage was increased slowly [see Clinical Studies (14.1)], syncope was reported in 0.4% (5/1,344) of iloperidone-treated patients (iloperidone and milsaperidone rapidly interconvert in vivo), compared with 0.2% (1/587) in placebo- treated patients. Orthostatic hypotension was reported in 5% of patients who received 20 mg to 24 mg/day of iloperidone, 3% of patients who received 10 mg to 16 mg/day of iloperidone, and 1% of patients who received placebo.
  • In a double-blind placebo-controlled short-term study in patients with bipolar mania (Study 4), syncope was reported in 0.5% (1/206) of iloperidone-treated patients with, compared with 0% (0/208) in placebo-treated patients. In Study 4, orthostatic hypotension was reported in 4% (9/206) of iloperidone-treated patients and 2% (5/208) of placebo-treated patients.

More rapid titration would be expected to increase the rate of orthostatic hypotension and syncope.

Orthostatic vital signs should be monitored in patients who are vulnerable to hypotension (e.g., elderly patients, patients with dehydration, hypovolemia, and concomitant treatment with antihypertensive drugs), patients with known cardiovascular disease (history of myocardial infarction, ischemic heart disease, heart failure, or conduction abnormalities), and patients with cerebrovascular disease.

5.8 Falls

Antipsychotics, including BYSANTI, may cause somnolence, postural hypotension, motor and sensory instability, which may lead to falls and, consequently, fractures or other injuries.

If patients have a condition or take concomitant drugs that could exacerbate these effects, complete fall risk assessments when initiating BYSANTI treatment and recurrently for patients on long-term treatment.

5.9 Seizures

Like other antipsychotic drugs, BYSANTI may cause seizures. The risk antipsychotic drug-associated is greatest in patients with a history of seizures or with conditions that lower the seizure threshold. Conditions that lower the seizure threshold may be more prevalent in older patients.

Use BYSANTI cautiously in patients with a history of seizures or with other conditions that lower seizure threshold.

5.10 Leukopenia, Neutropenia and Agranulocytosis

In clinical trial and postmarketing experience, leukopenia and neutropenia have been reported temporally related to antipsychotic drug treatment. Agranulocytosis (including fatal cases) has also been reported with antipsychotic drug use.

Possible risk factors for antipsychotic drug-associated leukopenia or neutropenia include preexisting low white blood cell count (WBC) or absolute neutrophil count (ANC) and history of drug induced leukopenia or neutropenia.

Patients with a pre-existing low WBC or ANC or a history of drug induced leukopenia or neutropenia should have frequently monitoring of their complete blood count (CBC) during the first few months of BYSANTI therapy and should discontinue BYSANTI at the first sign of a decline in WBC in the absence of other causative factors. Monitor patients with clinically significant neutropenia for fever or other symptoms or signs of infection and treat promptly if such symptoms or signs occur. Discontinue BYSANTI in patients with absolute ANC <1000/mm³ and follow their WBC until recovery.

5.11 Hyperprolactinemia

As with other drugs that antagonize dopamine D2 receptors, BYSANTI elevates prolactin levels. Hyperprolactinemia may suppress hypothalamic GnRH, resulting in reduced pituitary gonadotropin secretion. This, in turn, may inhibit reproductive function by impairing gonadal steroidogenesis in both female and male patients. Galactorrhea, amenorrhea, gynecomastia, and impotence have been reported with drugs associated with hyperprolactinemia. Long-standing hyperprolactinemia when associated with hypogonadism may lead to decreased bone density in both female and male patients.

Published epidemiologic studies have shown inconsistent results regarding the potential association between hyperprolactinemia and breast cancer.

Tissue culture experiments indicate that approximately one-third of human breast cancers are prolactin-dependent in vitro, a factor of potential importance if the use of a dopamine D2 receptor antagonist, including BYSANTI, is contemplated in a patient with previously detected breast cancer. Mammary gland proliferative changes and increases in serum prolactin were seen in mice and rats treated with iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) [see Nonclinical Toxicology (13)].

  • In a short-term placebo-controlled trial (4-weeks) in patients with schizophrenia (Study 2), the mean change from baseline to endpoint in plasma prolactin levels for the iloperidone 24 mg/day-treated group was an increase of 2.6 ng/mL compared to a decrease of 6.3 ng/mL in the placebo-group.
  • In placebo-controlled trials in adult patients with schizophrenia, elevated plasma prolactin levels (≥1.15xULN) were observed in 26% of iloperidone-treated patients compared to 12% of placebo-treated patients. In the short-term trials, iloperidone was associated with modest levels of prolactin elevation compared to greater prolactin elevations observed with some other antipsychotic drugs.
  • In pooled analysis from clinical studies including longer term trials, in 3,210 adults treated with iloperidone, gynecomastia was reported in 2 iloperidone-treated male patients (0.1%) compared to 0% in placebo-treated patients, and galactorrhea was reported in 8 iloperidone-treated female patients (0.2%) compared to 3 placebo- treated female patients (0.5%).
  • In a 4-week, placebo-controlled trial in patients with bipolar mania (Study 4), the mean change from baseline to endpoint in plasma prolactin levels for the iloperidone group was an increase of 15.7 ng/mL compared to a decrease of 0.6 ng/mL for the placebo group. In this trial, elevated plasma prolactin levels (≥1.15xULN) were observed in 35% of iloperidone-treated patients with compared to 1% of the placebo-treated patients.

5.12 Body Temperature Regulation

Atypical antipsychotics may disrupt the body's ability to reduce core body temperature. Strenuous exercise, exposure to extreme heat, dehydration, and anticholinergic medications may contribute to an elevation in core body temperature.

Use BYSANTI with caution in patients who may experience these conditions.

5.13 Dysphagia

Esophageal dysmotility and aspiration have been associated with antipsychotic drug use. Antipsychotic drugs, including BYSANTI, should be used cautiously in patients at risk for aspiration.

5.14 Priapism

In the clinical studies [see Clinical Studies (14)], three cases of priapism were reported in iloperidone-treated patients (iloperidone and milsaperidone rapidly interconvert in vivo) with schizophrenia and 1 case was reported in an iloperidone-treated patient with manic and mixed episodes associated with bipolar I disorder). Drugs with alpha- adrenergic blocking effects, including BYSANTI, have been reported to induce priapism. Severe priapism may require surgical intervention.

5.15 Potential for Cognitive and Motor Impairment

BYSANTI, like other antipsychotics, may cause somnolence and has the potential to impair judgment, thinking or motor skills. In short-term, placebo-controlled trials of schizophrenia in adults, somnolence (including sedation) was reported in 12% (104/874) of patients treated with iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) at dosage of 10 mg/day or greater versus 5.3% (31/587) of patients treated with placebo. In a short-term, placebo-controlled trial of bipolar mania (Study 4), somnolence (including sedation) was reported in 8% (16/206) of patients treated with iloperidone versus 3% (6/208) of patients treated with placebo.

Patients should be cautioned about driving a motor vehicle or operating hazardous machinery, until they are reasonably certain that therapy with BYSANTI does not adversely affect them.

5.16 Intraoperative Floppy Iris Syndrome

Intraoperative floppy iris syndrome has been observed during cataract surgery in some patients on or previously treated with alpha-1 adrenergic blockers. This variant of small pupil syndrome is characterized by the combination of a flaccid iris that billows in response to intraoperative irrigation currents, progressive intraoperative miosis despite preoperative dilation with standard mydriatic drugs, and potential prolapse of the iris toward the phacoemulsification incisions.

The initiation of therapy with BYSANTI in patients for whom cataract or glaucoma surgery is scheduled is not recommended. In patients taking or previously treated with alpha-1 adrenergic blockers, including BYSANTI, surgeons should be prepared for possible modifications to their surgical cataract technique, such as the utilization of iris hooks, iris dilator rings, or viscoelastic substances. There does not appear to be a benefit of stopping alpha1 blocker therapy prior to cataract surgery.

6. Adverse Reactions

The following adverse reactions are discussed in more detail in other sections of the labeling:

  • Increased Mortality in Elderly Patients with Dementia-Related Psychosis [see Warnings and Precautions (5.1)]
  • Cerebrovascular Adverse Reactions, Including Stroke, in Elderly Patients with Dementia-Related Psychosis [see Warnings and Precautions (5.2)]
  • QT Prolongation [see Warnings and Precautions (5.3)]
  • Neuroleptic Malignant Syndrome (NMS) [see Warnings and Precautions (5.4)]
  • Tardive Dyskinesia [see Warnings and Precautions (5.5)]
  • Metabolic Changes [see Warnings and Precautions (5.6)]
  • Orthostatic Hypotension and Syncope [see Warnings and Precautions (5.7)]
  • Falls [see Warnings and Precautions (5.8)]
  • Seizures [see Warnings and Precautions (5.9)]
  • Leukopenia, Neutropenia and Agranulocytosis [see Warnings and Precautions (5.10)]
  • Hyperprolactinemia [see Warnings and Precautions (5.11)]
  • Body Temperature Regulation [see Warnings and Precautions (5.12)]
  • Dysphagia [see Warnings and Precautions (5.13)]
  • Priapism [see Warnings and Precautions (5.14)]
  • Potential for Cognitive and Motor Impairment [see Warnings and Precautions (5.15)]
  • Intraoperative Floppy Iris Syndrome [see Warnings and Precautions (5.16)]

6.1. Clinical Trials Experience

Because clinical trials are conducted under widely varying conditions, adverse reaction rates observed in the clinical trial of a drug cannot be directly compared to rates in the clinical trials of another drug and may not reflect the rates observed in clinical practice.

The safety of BYSANTI has been established from adequate and well-controlled studies of iloperidone tablets (referred to hereafter as "iloperidone" (iloperidone and milsaperidone rapidly interconvert in vivo)) in adults with schizophrenia or with mixed or manic episodes associated with bipolar I disorder [see Clinical Studies (14.1, 14.2)]. Below is a display of the adverse reactions of iloperidone in these adequate and well-controlled studies.

The information below is derived from a clinical trial database for iloperidone that consisted of:

  • 3,229 adult patients exposed to iloperidone at a dosage of 10 mg/day or greater, for the treatment of schizophrenia which included 874 patients with schizophrenia in Studies 1, 2, and 3 [see Clinical Studies (14.1)] and another schizophrenia study and
  • 312 adult patients exposed to iloperidone at a dosages of 24 mg/day, for the acute treatment of manic or mixed episodes associated with bipolar I disorder (Study 4) [see Clinical Studies (14.2)].

Of these, 999 patients received iloperidone for at least 6 months, with 657 patients exposed to iloperidone for at least 12 months for the treatment of schizophrenia; and 69 patients received iloperidone for at least 6 months (with 28 patients received iloperidone for at least 12 months) for the treatment of bipolar mania. The conditions and duration of treatment with iloperidone varied and included (in overlapping categories), open-label and double-blind phases of studies, inpatients and outpatients, fixed-dose and flexible-dose studies, and studies with short-term or longer-term exposure.

Common Adverse Reactions in Adult Patients with Schizophrenia

The information presented below was derived from pooled data from 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies in adult patients with schizophrenia who received iloperidone at daily dosages within a range of 10 to 24 mg (n=874) (Studies 1, 2, and 3, and another study in schizophrenia) [see Clinical Studies (14.1)].

Table 3 displays adverse reactions that occurred in 2% or more of patients treated with iloperidone in any of the dosing groups, and for which the incidence in iloperidone-treated patients in any dosing group was greater than the incidence in placebo-treated patients in these studies.

Adverse reactions that occurred in ≥5% in the iloperidone-treated patients and at least twice that in placebo-treated patients included dizziness, dry mouth, fatigue, nasal congestion, somnolence, tachycardia, orthostatic hypotension, and weight increased.

Table 3. Percentage of Adverse Reactions in Short-Term, Fixed- or Flexible-Dose, Placebo-Controlled Schizophrenia Trials in Adult Patients*:

 Placebo
(N=587)
Iloperidone
10-16 mg/day
(N=483)
Iloperidone
20-24 mg/day
(N=391)
Dizziness7%10%20%
Somnolencea5%9%15%
Tachycardiab1%3%12%
Dry Mouth1%8%10%
Nausea8%7%10%
Weight Increased1%1%9%
Nasal Congestion2%5%8%
Diarrhea4%5%7%
Fatigue3%4%6%
Orthostatic Hypotension1%3%5%
Extrapyramidal Disorder4%5%4%
Nasopharyngitis3%4%3%
Arthralgia2%3%3%
Tremor2%3%3%
Upper Respiratory Tract
Infection
1%2%3%
Abdominal Discomfort1%1%3%
Hypotension<1%<1%3%
Musculoskeletal Stiffness1%1%3%
Ejaculation Failure<1%2%2%
Dyspnea<1%2%2%
Rash2%3%2%
Lethargy1%3%1%
Vision Blurred2%3%1%

* Includes adverse reactions that were reported in 2% or more of patients in any of the iloperidone dosing group and at greater incidence than in the placebo group. Figures rounded to the nearest integer.
a Somnolence includes somnolence and sedation
b Tachycardia includes tachycardia and heart rate increased

Common Adverse Reactions in Adult Patients with Bipolar Mania

Table 4 displays the adverse reactions that occurred at an incidence of ≥2% in iloperidone-treated patients and greater than in placebo-treated patients in a placebo-controlled, 4-week bipolar mania trial (Study 4) [see Clinical Studies (14.2)].

In Study 4, the following adverse reactions occurred in ≥5% in the iloperidone- treated patients and at least twice placebo-treated patients: tachycardia, dizziness, dry mouth, hepatic enzymes increased, nasal congestion, weight increased, hypotension, and somnolence.

Table 4. Adverse Reactions that Occurred in Adult Patients in a Short-Term, Fixed-Dose, Placebo-Controlled Bipolar Mania Trial (Study 4)*:

 Placebo
(N=208)
Iloperidone
24 mg/day**
(N=206)
Tachycardiaa5%23%
Dizzinessb1%12%
Dry mouth2%9%
Hepatic enzyme increasedc1%8%
Somnolenced3%8%
Hypotensione3%6%
Nasal congestion1%6%
Weight increasedf1%6%
Headacheg4%5%
Nauseah3%4%
Sexual Dysfunctioni<1%4%
Akathisia0%4%
Fatiguej1%3%
Urinary urgency and Polyuriak0%3%

* Adverse reactions occurring at an incidence of ≥2% in iloperidone-treated patients and greater than in placebo-treated patients. Figures rounded to the nearest integer.
** Patients with poor CYP2D6 metabolizer status received 12 mg/day.
a Tachycardia includes postural orthostatic tachycardia syndrome and other similar terms
b Dizziness includes postural dizziness
c Hepatic enzyme increased includes: predominantly alanine aminotransferase increased, aspartate aminotransferase increased, and transaminase increased
d Somnolence includes other similar terms
e Hypotension includes: orthostatic hypotension
f Weight increased includes other similar terms
g Headache includes tension headache
h Nausea includes vomiting
i Sexual Dysfunction includes: ejaculation failure, erectile dysfunction, retrograde ejaculation, and ejaculation delayed
j Fatigue includes similar terms
k Urinary urgency and polyuria includes: hypertonic bladder, micturition urgency, and urinary incontinence

Dose-Related Adverse Reactions in the Schizophrenia Studies

Based on the pooled data from 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies in patients with schizophrenia, adverse reactions that occurred with a greater than 2% incidence in iloperidone-treated patients, and for which the incidence in patients treated with iloperidone 20-24 mg/day were twice than the incidence in patients treated with iloperidone 10-16 mg/day were abdominal discomfort, dizziness, hypotension, musculoskeletal stiffness, tachycardia, and weight increased. Dizziness, tachycardia, and increased weight were at least twice as common on in patients treated with 20-24 mg/day as those treated with 10-16 mg/day.

Extrapyramidal Symptoms in the Schizophrenia and Bipolar Mania Studies

Table 5 displays treatment emergent extrapyramidal symptoms (EPS)-related events in the 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies in patients with schizophrenia.

Table 5. Percentage of Treatment Emergent EPS-Related Events in 4- or 6-week Schizophrenia Trials:

Preferred TermPlacebo
(N=587)
Iloperidone
10-16 mg/day
(N=483)
Iloperidone
20-24 mg/day
(N=391)
All EPS events11.6%13.5%15.1%
Tremor1.9%2.5%3.1%
Akathisia2.7%1.7%2.3%
Dyskinesia1.5%1.7%1%
Dystonia0.7%1%0.8%
Bradykinesia0%0.6%0.5%
Parkinsonism0%0.2%0.3%

Table 6 shows the percentage of treatment emergent EPS-related events in a 4-week bipolar mania trial.

Table 6. Percentage of Treatment Emergent EPS-Related Events in a 4-week Bipolar Mania Trial:

Preferred TermPlacebo
N=208
Iloperidone 24 mg/day*
N=206
All EPS events0% 8.3%
Akathisia0%4.4%
Extrapyramidal Disorder0%1%
Blepharospasm0%0.5%
Dystonia0%0.5%
Muscle Spasm0%0.5%
Restlessness0%0.5%
Torticollis0%0.5%
Tremor0%0.5%

* Patients with poor CYP2D6 metabolizer status received 12 mg/day.

Discontinuation of Treatment Due to Adverse Reactions in the Schizophrenia and Bipolar Mania Studies

Based on the pooled data from 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies in patients with schizophrenia (Studies 1, 2, 3, and another study), there was no difference in the incidence of discontinuation due to adverse reactions between iloperidone-treated patients (5%) and placebo-treated patients (5%). The types of adverse reactions that led to discontinuation were similar for the iloperidone- and placebo-treated patients.

In a 4-week, placebo-controlled study in patients with bipolar mania (Study 4), the incidence of discontinuation due to adverse reactions was higher in iloperidone-treated patients (8.7%) than placebo-treated patients (5.3%). Adverse reactions that led to discontinuation in more than one iloperidone-treated patient were liver enzyme elevations, nausea and vomiting, dizziness and hypotension.

Adverse Reactions by Demographic Groups in the Schizophrenia Studies

An examination of population subgroups in the 4 placebo-controlled, 4- or 6-week, fixed- or flexible-dose studies of patients with schizophrenia (Studies 1, 2, 3, and another study) did not reveal any evidence of differences in safety of iloperidone on the basis of age, sex or race.

Laboratory Test Abnormalities in the Schizophrenia and Bipolar Mania Studies

There were no differences between the iloperidone and placebo groups in the incidence of discontinuation due to changes in hematology laboratory tests, or urinalysis.

Elevated Serum Transaminases: In a short-term placebo-controlled trial in patients with bipolar mania (Study 4), asymptomatic alanine aminotransferase (ALT) elevations ≥3x ULN occurred in 9.2% of iloperidone-treated patients compared to 1.5% of placebo-treated patients. AST elevations were less common.

Decreased Hematocrit: In short-term placebo-controlled trials (4- to 6-weeks) in patients with schizophrenia, 1% (13/1,342) of iloperidone-treated patients had a hematocrit at least one time below the extended normal range during post-randomization treatment, compared to 0.3% (2/585) of placebo-treated patients. The extended normal range for lowered hematocrit was defined in each of these trials as the value 15% below the normal range for the centralized laboratory that was used in the trial.

In a short-term placebo-controlled trial (4 weeks) in patients with bipolar mania (Study 4), 3.5% (7/200) of iloperidone-treated patients had a hematocrit at least one time below the extended normal range (<0.85xLLN) during post- randomization treatment, compared to 0.5% (1/196) of placebo-treated patients.

Analysis of clinical laboratory data following iloperidone administration suggested that decreases in hematocrit, hemoglobin, white blood cells, total protein, and albumin were due to hemodilution. Decreases in hematocrit and total protein have been observed with other alpha receptor antagonists and are attributed to hemodilution [see Clinical Pharmacology (12.2)].

Elevated Serum Urate Levels: In a 4-week placebo-controlled trial in patients with schizophrenia (Study 2), treatment with iloperidone 12 mg twice a day resulted in an increase of serum urate levels of approximately 28 μmol/L (0.471 mg/dL) compared to an increase of 4.2 μmol/L (0.07 mg/dL) with treatment with placebo.

In a 4-week placebo-controlled trial in patients with bipolar mania (Study 4), treatment with iloperidone 12 mg twice a day resulted in an increase of serum urate levels of approximately 27.2 μmol/L (0.457 mg/dL) compared to an increase of 0.1 μmol/L (0.002 mg/dL) to treatment with placebo.

Other Reactions During the Pre-marketing Evaluation of Iloperidone in the Schizophrenia Studies

The following is a list additional adverse reactions (not listed above) in patients with schizophrenia treated with iloperidone (n=3,210) at multiple doses ≥ 4 mg/day.

Reactions are listed in order of decreasing frequency according to the following definitions: frequent adverse events were those that occurred in at least 1/100 patients (only those not listed in Table 3 appear in this listing); infrequent adverse reactions were those that occurred in 1/100 to 1/1,000 patients; and rare events were those that occurred in fewer than 1/1,000 patients.

  • Blood and Lymphatic Disorders: Infrequent – anemia, iron deficiency anemia; Rare – leukopenia
  • Cardiac Disorders: Frequent – palpitations; Rare – arrhythmia, atrioventricular block first degree, cardiac failure (including congestive and acute)
  • Ear and Labyrinth Disorders: Infrequent – vertigo, tinnitus
  • Endocrine Disorders: Infrequent – hypothyroidism
  • Eye Disorders: Frequent – conjunctivitis (including allergic); Infrequent – dry eye, blepharitis, eyelid edema, eye swelling, lenticular opacities, cataract, hyperemia (including conjunctival)
  • Gastrointestinal Disorders: Infrequent – gastritis, salivary hypersecretion, fecal incontinence, mouth ulceration; Rare – aphthous stomatitis, duodenal ulcer, hiatus hernia, hyperchlorhydria, lip ulceration, reflux esophagitis, stomatitis
  • General Disorders and Administrative Site Conditions: Infrequent – edema (general, pitting, due to cardiac disease), difficulty in walking, thirst; Rare – hyperthermia
  • Hepatobiliary Disorders: Infrequent – cholelithiasis
  • Investigations: Frequent: weight decreased; Infrequent – hemoglobin decreased, neutrophil count increased, hematocrit decreased
  • Metabolism and Nutrition Disorders: Infrequent – increased appetite, dehydration, hypokalemia, fluid retention
  • Musculoskeletal and Connective Tissue Disorders: Frequent – myalgia, muscle spasms; Rare – torticollis
  • Nervous System Disorders: Infrequent – paresthesia, psychomotor hyperactivity, restlessness, amnesia, nystagmus; Rare – restless legs syndrome
  • Psychiatric Disorders: Frequent – restlessness, aggression, delusion; Infrequent – hostility, libido decreased, paranoia, anorgasmia, confusional state, mania, catatonia, mood swings, panic attack, obsessive-compulsive disorder, bulimia nervosa, delirium, polydipsia psychogenic, impulse-control disorder, major depression
  • Renal and Urinary Disorders: Frequent – urinary incontinence; Infrequent – dysuria, pollakiuria, enuresis, nephrolithiasis; Rare – urinary retention, renal failure acute
  • Reproductive System and Breast Disorders: Frequent – erectile dysfunction; Infrequent – testicular pain, amenorrhea, breast pain; Rare – menstruation irregular, gynecomastia, menorrhagia, metrorrhagia, postmenopausal hemorrhage, prostatitis
  • Respiratory, Thoracic and Mediastinal Disorders: Infrequent – epistaxis, asthma, rhinorrhea, sinus congestion, nasal dryness; Rare – dry throat, sleep apnea syndrome, dyspnea exertional

6.2. Postmarketing Experience

The following adverse reactions have been identified during post-approval use of iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo). Because these reactions are reported voluntarily from a population of uncertain size, it is not always possible to estimate their frequency or establish a causal relationship to drug exposure: retrograde ejaculation and hypersensitivity reactions (including anaphylaxis; angioedema; throat tightness; oropharyngeal swelling; swelling of the face, lips, mouth, and tongue; urticaria; rash; and pruritus).

7. Drug Interactions

7.1 Effects of Other Drugs on BYSANTI

Table 7 presents clinically significant drug interactions where concomitant use of another drug affects BYSANTI.

Table 7. Clinically Significant Drug Interactions: Concomitant Use of Other Drugs Affect the Use of BYSANTI:

Strong CYP2D6 Inhibitors
Prevention or
Management
• Reduce the dosage of BYSANTI when administered with a strong CYP2D6
inhibitor [see Dosage and Administration (2.4)].
• When the strong CYP2D6 inhibitor is stopped in BYSANTI-treated patients,
gradually increase the BYSANTI dosage to the pre-inhibitor dosage.
Mechanism and
Clinical Effect(s)
Milsaperidone and iloperidone are CYP2D6 substrates (iloperidone and milsaperidone
rapidly interconvert in vivo). Strong CYP2D6 inhibitors increased exposure of
milsaperidone and iloperidone [see Clinical Pharmacology (12.3, 12.5)], which may
increase the risk of BYSANTI-associated adverse reactions.
Strong CYP3A4 Inhibitors
Prevention or
Management
• Reduce the dosage of BYSANTI when administered with a strong CYP3A4
inhibitor [see Dosage and Administration (2.4)].
• When the strong CYP3A4 inhibitor is stopped in BYSANTI-treated patients,
gradually increase the BYSANTI dosage to the pre-inhibitor dosage.
Mechanism and
Clinical Effect(s)
Milsaperidone and iloperidone are CYP3A4 substrates. Strong CYP3A4 inhibitors
increased the exposure of milsaperidone, iloperidone and P95 [see Clinical
Pharmacology (12.3)]
, which may increase the risk of BYSANTI-associated adverse
reactions.
Strong CYP2D6 and Strong CYP3A4 Inhibitors
Prevention or
Management
Reduce the dosage of BYSANTI if administered concomitantly with both a strong
CYP2D6 inhibitor and a strong CYP3A4 inhibitor.
Mechanism and
Clinical Effect(s)
Concomitant administration with a strong CYP2D6 inhibitor and a strong CYP3A4
inhibitor resulted in an increase in steady-state exposure of milsaperidone and
iloperidone [see Clinical Pharmacology (12.3)], which may increase the risk of
BYSANTI-associated adverse reactions.

7.2 Drugs that Prolong the QTc Interval

Avoid concomitant use of BYSANTI with other drugs that prolong the QTc interval [see Warnings and Precautions (5.3)].

Iloperidone causes QTc interval prolongation [see Clinical Pharmacology (12.2)]. Concomitant use of BYSANTI with other drugs that prolong the QTc interval may result in a greater increase in the QTc interval and adverse reactions associated with QTc interval prolongation, including arrhythmias.

7.3 Drugs that Lower Blood Pressure

Concomitant use of BYSANTI with drugs that lower blood pressure could potentially cause symptomatic hypotension. Avoid concomitant administration of BYSANTI with alpha-adrenergic blocking agents and consider lowering the dosage of other drugs that lower blood pressure [see Warnings and Precautions (5.7)].

8.1. Pregnancy

Pregnancy Exposure Registry

There is a pregnancy exposure registry that monitors pregnancy outcomes in women exposed to BYSANTI during pregnancy. For more information contact the National Pregnancy Registry for Atypical Antipsychotics at 1-866-961-2388 or visit http://womensmentalhealth.org/clinical-and-research-programs/pregnancyregistry/.

Risk Summary

Neonates exposed to antipsychotic drugs, including BYSANTI, during the third trimester of pregnancy are at risk for extrapyramidal and/or withdrawal symptoms following delivery (see Clinical Considerations). There are no available data with BYSANTI use during pregnancy and available data from pharmacovigilance reports with iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) use during pregnancy are insufficient to inform a drug-associated risk for major birth defects and miscarriage. There are risks to the mother associated with untreated schizophrenia or bipolar I disorder (see Clinical Considerations).

When iloperidone) was administered orally to pregnant rats during organogenesis at doses up to 26 times the maximum recommended human dose (MRHD) of 24 mg/day on mg/m² basis it prolonged the duration of pregnancy and parturition, increased still births, early intrauterine deaths, increased incidence of developmental delays, and decreased post-partum pup survival. When iloperidone was administered orally to pregnant rabbits during organogenesis at doses up to 20-times the MRHD on mg/m² basis it increased early intrauterine deaths and decreased fetal viability at term at the highest dose which was also a maternally toxic dose (see Data). The safety margins for milsaperidone are expected to be the same as those seen with iloperidone because exposures to iloperidone, milsaperidone, and their major metabolites are similar when either iloperidone tablets or BYSANTI (milsaperidone) tablets are administered in humans.

The background risk of major birth defects and miscarriage in patients with schizophrenia or bipolar disorder is unknown. In the U.S. general population, the estimated background risk of major birth defects and miscarriage in clinically recognized pregnancies is 2 to 4% and 15 to 20%, respectively.

Clinical Considerations

Disease-Associated Maternal and/or Embryo/Fetal Risk: There is a risk to the mother from untreated schizophrenia or bipolar I disorder, including increased risk of relapse, hospitalization, and suicide. Schizophrenia and bipolar I disorder are associated with increased adverse perinatal outcomes, including preterm birth. It is not known if this is a direct result of the illness or other comorbid factors.

Fetal/Neonatal Adverse Reactions: Extrapyramidal and/or withdrawal symptoms, including agitation, hypertonia, hypotonia, tremor, somnolence, respiratory distress and feeding disorder have been reported in neonates whose mothers were exposed to antipsychotic drugs during the third trimester of pregnancy. These symptoms have varied in severity.

Some neonates recovered within hours or days without specific treatment; others required prolonged hospitalization. Monitor neonates for extrapyramidal and/or withdrawal symptoms and manage symptoms appropriately.

Data

Animal Data: In an embryo-fetal development study, pregnant rats were given 4, 16, or 64 mg/kg/day (1.6, 6.5, and 26 times the maximum recommended human dose (MRHD) of 24 mg/day on a mg/m² basis) of iloperidone orally during the period of organogenesis. The highest dose caused increased early intrauterine deaths, decreased fetal weight and length, decreased fetal skeletal ossification, and an increased incidence of minor fetal skeletal anomalies and variations; this dose also caused decreased maternal food consumption and weight gain.

In an embryo-fetal development study, pregnant rabbits were given 4, 10, or 25 mg/kg/day (3, 8, and 20 times the MRHD on a mg/m² basis) of iloperidone during the period of organogenesis. The highest dose caused increased early intrauterine deaths and decreased fetal viability at term; this dose also caused maternal toxicity.

In additional studies in which rats were given iloperidone at doses similar to the above beginning from either pre-conception or from day 17 of gestation and continuing through weaning, adverse reproductive effects included prolonged pregnancy and parturition, increased stillbirth rates, increased incidence of fetal visceral variations, decreased fetal and pup weights, and decreased post-partum pup survival. There were no drug effects on the neurobehavioral or reproductive development of the surviving pups. No-effect doses ranged from 4 to 12 mg/kg except for the increase in stillbirth rates which occurred at the lowest dose tested of 4 mg/kg, which is 1.6 times the MRHD on a mg/m² basis. Maternal toxicity was seen at the higher doses in these studies.

The iloperidone metabolite P95, which is a major circulating metabolite of iloperidone in humans but is not present in significant amounts in rats, was given to pregnant rats during the period of organogenesis at oral doses of 20, 80, or 200 mg/kg/day. No teratogenic effects were seen. Delayed skeletal ossification occurred at all doses. No significant maternal toxicity was produced. Plasma levels of P95 (AUC) at the highest dose tested were 2 times those in humans receiving the MRHD of iloperidone.

8.2. Lactation

Risk Summary

There are no data on the presence of milsaperidone or its major metabolite, P95, in either human or animal milk, the effects on the breastfed infant, or the effects on milk production. Iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) is present in rat milk following iloperidone administration (see Data). When a drug is present in animal milk, it is likely to be present in human milk. Because of the potential for serious adverse reactions in the breastfed infant, advise patients not to breastfeed during BYSANTI treatment and for 6 days after the last dose in CYP2D6 normal metabolizers and 8 days after the last dose in CYP2D6 poor metabolizers.

Data

The transfer of radioactivity into the milk of lactating rats was investigated following a single dose of [14C] iloperidone at 5 mg/kg. The concentration of radioactivity in milk at 4 hours post-dose was near 10-fold greater than that in plasma at the same time. However, by 24 hours after dosing, concentrations of radioactivity in milk had fallen to values slightly lower than plasma. The metabolic profile in milk was qualitatively similar to that in plasma.

8.4. Pediatric Use

Safety and effectiveness of BYSANTI have not been established in pediatric patients.

8.5. Geriatric Use

Clinical studies of iloperidone (iloperidone and milsaperidone rapidly interconvert in vivo) in the treatment of schizophrenia did not include sufficient numbers of patients aged 65 years and over to determine whether or not they respond differently than younger adult patients. Of the 3,210 patients with schizophrenia treated with iloperidone in clinical trials, 25 (0.5%) were ≥65 years old and there were no patients ≥75 years old. Of the 206 patients with bipolar mania treated with iloperidone in a clinical trial (Study 4), 2 (0.1%) were 65 years old and there were no patients were >75 years old.

Elderly patients with dementia-related psychosis treated with BYSANTI are at an increased risk of death compared to placebo. BYSANTI is not approved for the treatment of patients with dementia-related psychosis [see Boxed Warning and Warnings and Precautions (5.1, 5.2)].

Elderly patients with dementia-related psychosis treated with antipsychotics have an increased risk of cerebrovascular adverse reactions (e.g., stroke, transient ischemic attack) including fatalities, compared to those treated with placebo [see Warnings and Precautions (5.2)].

Antipsychotic drugs increase the risk of tardive dyskinesia, and this risk appears to be highest among the elderly, particularly elderly women [see Warnings and Precautions (5.5)].

8.7. Hepatic Impairment

The recommended BYSANTI dosage in patients with mild hepatic impairment (HI) (Child-Pugh class A) is the same as those with normal hepatic function. Consider a lower dosage in patients with moderate HI (Child-Pugh class B). BYSANTI is not recommended in patients with severe HI (Child-Pugh class C) [see Dosage and Administration (2.3) and Clinical Pharmacology (12.3)].

Milsaperidone exposure was increased in patients with moderate HI [see Clinical Pharmacology (12.3)], which may increase the risk of BYSANTI-associated adverse reactions.

8. Use in Specific Populations

8.7 Use in Genomic Subgroups

The recommended BYSANTI dosage in CYP2D6 poor metabolizers is lower than the recommended dosage in the overall population [see Dosage and Administration (2.2)]. The plasma concentrations of milsaperidone are elevated in CYP2D6 poor metabolizers which may increase the risk of BYSANTI adverse reactions [see Warnings and Precautions (5.3) and (5.7)].

The prevalence of CYP2D6 poor metabolizers is approximately 7% in White population, 2% in Asian population, and 2% in Black or African American population.

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